Learn About Duchenne Clinical Trials From Top to Bottom
Duchenne muscular dystrophy is a rare genetic disease. It is also referred to as DMD or just Duchenne. It mostly affects men, rarely women. DMD weakens and damages the muscles. Life expectancy is 26, although in some cases it can be 30 or 40. There is currently no cure for this degenerative disease—only treatment that alleviates the symptoms. This is one of the main reasons people consider joining a Duchenne clinical trial.
What Are Duchenne Muscular Dystrophy Clinical Trials?
Research centers conduct Duchenne clinical trials to try to find the cure but also to test new treatments and drugs that could treat symptoms more effectively.
There are various DMD clinical trials designed for different participants, study types, and clinical trial phases.
Who Can Participate in DMD Clinical Trials?
Three kinds of participants may be eligible for a Duchenne medical trial:
- Healthy volunteers—They can usually participate in Phase I DMD trials
- People who suffer from DMD
- Female carriers of DMD
What DMD Study Types Are There?
When you browse clinical trials, you could also consider different types:
- Randomized—Participants are divided into groups and receive different treatments
- Double-blind—Neither the medical professionals nor the volunteers know who is getting a placebo
- Observational—They optimize testing procedures, examining better ways to detect the disease
- Treatment—Medical professionals analyze and test new drugs, treatment, radiation therapy, and surgery procedures
- Genetic—Gene changes that cause the disease are examined in this clinical trial
What Are Clinical Trial Phases?
After lab research and animal testing, the Food and Drug Administration (FDA) needs to approve a clinical trial with human participants. Once it sets off, a clinical trial can start going through phases, which the FDA also has to authorize.
Phase | Description | Number of Participants |
Phase 0 |
|
10–15 |
Phase I |
|
15–30 |
Phase II |
|
50–300 |
Phase III |
|
More than 100 |
Phase IV |
|
Hundreds to thousands |
DoNotPay Can Help You Find and Sign Up for DMD Clinical Trials!
Googling “clinical trials near me,” comparing them, and deciding which one is right for you or your loved one can be challenging. DoNotPay can fast-track your search and find the clinical trials best suited for your preferences.
Open DoNotPay in any web browser and do the following:
- Select Clinical Trials
- Click on Get Started and apply filters
- Tap on the trial of your choice
- Hit Contact Now
That’s all you have to do! We will then email the research center on your behalf and start the enrollment process.
Other perks of using DoNotPay as your clinical study search tool include:
- No fees
- Regularly updated homepage
- Extensive database of clinical trials
- Wide array of university psychology studies and paid medical surveys
- Limitless clinical study signups
- Handy bookmarking feature to save and browse clinical trials with ease
- Smart text alerts to let you know when a new clinical study starts recruiting
- Continuous tracking of clinical trials you signed up for
- Vast range of filters such as your age, location, medical condition, and compensation
Why Should I Join a Clinical Trial?
Clinical trials are essential for the betterment of science and medicine. Every existing medication has had to go through meticulous research and tests.
As a healthy volunteer, your motives may be altruistic or financial. As a person who suffers from or whose loved one suffers from Duchenne muscular dystrophy, all the more reason to join a clinical trial. If DMD patients could get even the slightest chance of better quality of life, reduced symptoms, or an efficient cure, participating in clinical trials is definitely worthwhile.
The Pros and Cons of Taking Part in Clinical Trials
With all its many benefits for patients and medicine in general, clinical studies do have some drawbacks. You can compare the two before making an informed decision about signing up for a medical trial:
Pros | Cons |
|
|
What To Take Into Consideration Before Participating in a Clinical Study
Before you decide to sign up for a clinical trial, there are a few details to consider. Being a participant is a serious undertaking, and you should not take it lightly. Mull over these questions:
- Are clinical trials safe?
- Do I have time to dedicate myself fully to a clinical trial?
- Did I gather all the necessary information about the research center and the trial itself?
- Did I familiarize myself with the Informed Consent form?
- Do I qualify for a clinical trial?
- Did I talk to my doctor about whether I should join a trial?
How Else Can I Find Duchenne Clinical Trials?
If you’re interested in other ways you can search for DMD clinical studies, you should consider some of these websites:
Website | Key Features | Instructions |
|
| |
|
|
What To Expect From DMD Clinical Studies
When a research center representative reaches out to you after your application, they could ask you additional questions to determine your eligibility. Afterward, you will have to go through a screening process. This may include various check-ups and tests. All clinical trial participants must meet both the inclusion and exclusion criteria based on your age, background, medical condition, etc.
The next step in the process of enrollment is Informed Consent. Its purpose is to inform you about the ins and outs of the clinical trial and its possible risks.
How Long Does a DMD Clinical Trial Last?
There is no unified length of any clinical trial. This can depend on factors such as the trial type—e.g., Observational or Treatment—and the number of participants.
What Is Expected of a Participant?
You may have to travel if a research center isn’t near you, or you might stay there until the conclusion of the trial. Medical professionals could ask you to keep a log to report on your daily life during the clinical study.
You are allowed to change your mind at any time and leave the research center.
DoNotPay Is Adept at Cutting Through the Red Tape!
DoNotPay can help you find other clinical trials as well. We have compiled a clinical trial database in states such as Ohio, Utah, Texas, Arizona, and North Carolina. Matching you or your loved one with a suitable clinical trial is not all we can do for you.
Freeing you from administrative issues is also our mission. Access DoNotPay from your web browser and browse our nifty solutions:
- Starting free trials risk-free
- Overturning your traffic tickets
- Finding other clinical trials
- Contesting speeding tickets
- Challenging parking citations
- Handling credit card issues
- Taking anyone to small claims court
- Getting help with unpaid bills
- Protecting yourself from stalking and harassment
- Claiming a refund from any company
- Blocking spam text messages
- Doing away with spam emails forever
- Protecting your work against copyright infringement
- Jumping the queue when calling customer service
- Getting revenge on annoying robocalls
- Scheduling a DMV appointment in no time
- Ending unwanted subscriptions and memberships
- Requesting refunds and compensation for delayed or canceled flights